Our Patients
Educational Resources and Advocacy
We are committed allies in easing the burden of living with rare endocrine diseases. In addition to our mission of bringing novel treatments to patients and their families, we believe in supporting the needs of the communities we serve.
We are proud to work with advocacy and educational organizations to support patients and families with rare endocrine diseases.
Additional patient and family resources can be found through the following organizations:
Rare Disease
Global Genes
National Organization for Rare Disorders (NORD)
Prader-Willi Syndrome (PWS)
Foundation for Prader-Willi Research (FPWR)
International Prader-Willi Syndrome Organisation (IPWSO)
Prader-Willi Syndrome Association (PWSA)
PWS Clinical Trial Consortium (PWS CTC)
Classic Congenital Adrenal Hyperplasia (CAH)
CARES Foundation
